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Events & Presentations

Events & Presentations

Presentations

Date Documents
Dec 3, 2019
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    Corporate Presentation 3 MB
Apr 17, 2019
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    Analyst Day Presentation 11.4 MB

Upcoming Events

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Archived Events

Date Event Details
Summary Toggle Dec 4, 2019
2:00 PM EST
Piper Jaffray 31ST Annual Healthcare Conference

Location

New York, NY
Listen to webcast
Summary Toggle Nov 20, 2019
1:50 PM EST
Stifel Healthcare Conference

Presentation by Tom Kassberg, the company’s Chief Business Officer.

Location

New York, NY
Listen to webcast
Summary Toggle Nov 12, 2019
11:30 AM MST
Credit Suisse 28TH Annual Healthcare Conference
Presentation by Emil D. Kakkis, M.D., Ph.D., the company's Chief Executive Officer.

Location

Scottsdale, Arizona
Listen to webcast
Summary Toggle Nov 5, 2019
5:00 PM EST
Third Quarter 2019 Financial Results and Corporate Update
Listen to webcast
Summary Toggle Oct 8, 2019
9:45 AM EDT
Jefferies Gene Therapy/Editing Summit

Location

New York, NY
Listen to Webcast
Summary Toggle Sep 11, 2019
2:10 PM EDT
Morgan Stanley 17TH Annual Global Healthcare Conference

Location

New York, NY
Listen to Webcast
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    • Management
      • Emil D. Kakkis, M.D., Ph.D.
      • Jayson Dallas, M.D.
      • Dennis Huang
      • Thomas Kassberg
      • Karah Parschauer
      • John Pinion
      • Shalini Sharp
    • Board of Directors
      • Daniel G. Welch
      • Emil D. Kakkis, M.D., Ph.D.
      • William Aliski
      • Deborah Dunsire, M.D.
      • Lars Ekman, M.D., Ph.D.
      • Matthew K. Fust
      • Michael Narachi
      • Clay B. Siegall, Ph.D.
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    • Management
      • Emil D. Kakkis, M.D., Ph.D.
      • Jayson Dallas, M.D.
      • Dennis Huang
      • Thomas Kassberg
      • Karah Parschauer
      • John Pinion
      • Shalini Sharp
    • Board of Directors
      • Daniel G. Welch
      • Emil D. Kakkis, M.D., Ph.D.
      • William Aliski
      • Deborah Dunsire, M.D.
      • Lars Ekman, M.D., Ph.D.
      • Matthew K. Fust
      • Michael Narachi
      • Clay B. Siegall, Ph.D.
    • Grants & Charitable Contributions
    • Message from BIO
    • Medicines
      • Crysvita®
      • Mepsevii™
  • Pipeline
    • Burosumab for XLH
    • Burosumab for TIO
    • Vestronidase alfa
    • UX007 for FAOD
    • UX007 for Glut1 DS
    • DTX 301 for OTC
    • DTX 401 for GSD1a
    • Presentations & Publications
  • For Patients
    • XLH
    • TIO
    • MPS 7
    • LC-FAOD
    • Glut1 DS
    • OTC
    • GSD1a
    • Access to Approved Therapies
    • Access to Investigational Therapies
  • Investors

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